Gene Therapy Company Born from Mother's Quest to Cure Daughter
RARECast - A podcast by RARECast - Thursdays
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When Karen Aiach’s daughter was diagnosed with Sanfilippo Syndrome A, a rare neurodegenerative disease, she and her husband established a nonprofit to fund research. Eventually, as the work progressed, they launched Lysogene, a biotechnology company focused on gene therapy. We spoke to Aiach, CEO of Lysogene, about Sanfilippo Syndrome A, why the focus on gene therapy, and the progress the company has made to date.