RARECast

548 Episodes

1. Forging a Research Agenda for a Rare Disease

   Published: 7/25/2018
2. Making the Journey from All-American Athlete to Rare Disease Advocate

   Published: 7/18/2018
3. How Destiny Lamonte Learned to Advocate for Herself and Others

   Published: 7/11/2018
4. Where the NIH Does Its Banking

   Published: 7/5/2018
5. Making Sense of Nonsense Mutations

   Published: 6/27/2018
6. Rewriting Faulty RNA

   Published: 6/20/2018
7. Experimental Drug for "Elephant Man" Disease May Benefit Certain Cancers Too

   Published: 6/13/2018
8. Programming Stem Cells to Protect Neurons in ALS and other Neurodegenerative Conditions

   Published: 6/6/2018
9. Why a Topical, Off-the-Shelf, Gene Therapy May Hold Promise for a Rare Skin Condition

   Published: 5/30/2018
10. An Ironman Champion with Cystic Fibrosis Discusses her Changing Relationship with Her Disease

    Published: 5/23/2018
11. Why an Experimental Fragile X Drug May Treat a Range of Neurodegenerative Diseases

    Published: 5/16/2018
12. The Case for a Daily Self-Injection to Treat Hemophilia

    Published: 5/9/2018
13. Addressing the Challenges of R&D for Rare Cancer Therapies

    Published: 5/2/2018
14. Learning to Communicate and Collaborate as a Patient Advocate

    Published: 4/25/2018
15. Seeking Answers for Undiagnosed Patients

    Published: 4/18/2018
16. When "Undiagnosed" Is Your Diagnosis

    Published: 4/11/2018
17. The Decision to Get Tested for Huntington's Disease and How It Changed Seth Rotberg's Life

    Published: 4/4/2018
18. Nonprofit Sees Need in Developing Gene Therapies for Inherited Eye Disesases

    Published: 3/29/2018
19. Casting a Wider Net for Genetic Diseases

    Published: 3/21/2018
20. Corbus Seeks to Quiet the Immune System in Chronic Conditions

    Published: 3/14/2018