RARECast

516 Episodes

1. FDA Outlines a Collaborative Approach for Pediatric Rare Disease Trials

   Published: 12/13/2017
2. Why Patient-Centred Outcomes Are Critical to Rare Disease Drug Trials

   Published: 12/6/2017
3. What the FDA's New Framework Means for Regenerative Therapies

   Published: 11/29/2017
4. Measuring the Value of Therapies for Ultra-Rare Diseases

   Published: 11/22/2017
5. Lessons from Pitching Venture Capitalists

   Published: 11/15/2017
6. Health Canada Scraps Plans for Orphan Drug Framework

   Published: 11/8/2017
7. New Investment Boosts Rare Disease Drug Accelerator

   Published: 11/1/2017
8. Understanding Rare Disease Caregiver Needs

   Published: 10/25/2017
9. Deriving Rare Disease Therapies from Human Plasma

   Published: 10/18/2017
10. Learning to Live with Purpose

    Published: 10/11/2017
11. A Mother's Race to Find a Treatment for Her Daughter's Ultra-Rare Condition

    Published: 10/4/2017
12. Screening for Rare Diseases

    Published: 9/27/2017
13. A Look at the Changing World of Work for People with a Chronic Illness

    Published: 9/20/2017
14. Aligning Interests in Rare Disease Partnerships

    Published: 9/13/2017
15. A Veteran Venture Capitalist Discusses Investing in Rare Disease Drug Development

    Published: 9/6/2017
16. A Patient Group Crafts Guidelines for Working with Pharma

    Published: 8/30/2017
17. Bringing Innovation to Business Models for Rare Disease Drug Development

    Published: 8/23/2017
18. Rethinking Accessibility and Dependency

    Published: 8/16/2017
19. How Simon Wheatcroft, Blinded by a Rare Disease, Became an Ultramarathoner

    Published: 8/9/2017
20. Spark Hoping Its Luxturna Will Become First FDA-Approved Gene Therapy

    Published: 8/2/2017