RARECast

548 Episodes

1. Navigating the Challenges of Rare Disease Drug Development

   Published: 5/31/2017
2. Accelerating Rare Disease Drug Discovery

   Published: 5/24/2017
3. Experimental Rare Disease Therapy Wins New FDA Reg Med Designation

   Published: 5/17/2017
4. How Rare Disease Patients Can Get their Voices Heard in Drug Discovery and Development

   Published: 5/10/2017
5. One Patient's Difficult Road to a Rare Diagnosis

   Published: 5/3/2017
6. How Researchers Diagnosed Four Patients with a Never-Before-Identified Rare Disease in a Day

   Published: 4/26/2017
7. Stem Cell Gene Therapy Restores Immune System in Kids with SCID

   Published: 4/19/2017
8. Rare Disease Advocates Push for Incentives to Drugmakers Pulled from Cures Act

   Published: 4/12/2017
9. Non-Profit Drug Company Seeks to Advance Rare Disease Therapies

   Published: 4/5/2017
10. Innovative Collaboration Model Drives Treatment for Rare Disease

    Published: 3/29/2017
11. Girl with Rare Disease Inspires Search for Bone Marrow Donors

    Published: 3/22/2017
12. A Quest for Tribe: Searching for Others with the Same Ultra-Rare Mutation

    Published: 3/15/2017
13. Raising Awareness in a Town with a History of a Rare Disease

    Published: 3/8/2017
14. Helping Rare Disease Patients Navigate the World of Information

    Published: 3/1/2017
15. Overcoming the Challenges of Rare Disease Drug Development

    Published: 2/22/2017
16. Moving Rare Disease Therapies from Hope to Reality

    Published: 2/15/2017
17. Children’s National Launches First-of-its-Kind Rare Disease Center

    Published: 2/8/2017
18. A Common Link in a Group of Rare Diseases Creates an Opportunity for Repurposing

    Published: 2/1/2017
19. Sobi Works to Expand Rare Disease Indications for Its Drugs

    Published: 1/25/2017
20. Why Rare Disease Patients Should Work Together to Address Common Concerns

    Published: 1/18/2017