RARECast

516 Episodes

1. Abeona Advancing Pipeline of Gene Therapies for Rare Diseases

   Published: 10/19/2016
2. A Patient Attends "an Academic Conference for Everyone"

   Published: 10/12/2016
3. Teen Advocate Preaches Message of Kindness

   Published: 10/6/2016
4. A Controversial Approval for a Duchenne Drug and What's Ahead

   Published: 9/28/2016
5. Matchmaker Exchange Helps Rare Disease Community Find Me a Find

   Published: 9/21/2016
6. The Promise of RNAi for Hereditary Angioedema and Other Rare Diseases

   Published: 9/14/2016
7. Why Natural History Studies Matter to Rare Disease Patients

   Published: 9/7/2016
8. Harnessing Big Data to Work for Rare Disease Patients

   Published: 8/31/2016
9. Lessons from Autism on Accelerating Drug Development

   Published: 8/24/2016
10. How One Rare Disease Group Leverages Relationships with Industry

    Published: 8/17/2016
11. Ice Bucket Challenge Begins to Yield Results

    Published: 8/10/2016
12. Why a Common Diabetes Drug May Be Able to Treat a Rare Disease

    Published: 8/3/2016
13. How to Improve Patient Access to Experimental Drugs

    Published: 7/27/2016
14. Using Social Media to Find Rare Disease Patients for Clinical Trials

    Published: 7/20/2016
15. How Rare Disease Patients Weigh Risks and Benefits of a Therapy

    Published: 7/13/2016
16. Why Homology Medicines Might Be a Game Changer for Gene Therapy

    Published: 7/6/2016
17. Orchard Hopes to Bear the Fruit of Gene Therapy

    Published: 6/28/2016
18. Novel Approach to Treat Rare Disease May Lead to Drugs for Common Ones

    Published: 6/22/2016
19. Brining Whole Genome Sequencing into the Clinic

    Published: 6/15/2016
20. Bringing Patient-Centricity to Clinical Trials

    Published: 6/8/2016