RARECast

512 Episodes

1. Matchmaker Exchange Helps Rare Disease Community Find Me a Find

   Published: 9/21/2016
2. The Promise of RNAi for Hereditary Angioedema and Other Rare Diseases

   Published: 9/14/2016
3. Why Natural History Studies Matter to Rare Disease Patients

   Published: 9/7/2016
4. Harnessing Big Data to Work for Rare Disease Patients

   Published: 8/31/2016
5. Lessons from Autism on Accelerating Drug Development

   Published: 8/24/2016
6. How One Rare Disease Group Leverages Relationships with Industry

   Published: 8/17/2016
7. Ice Bucket Challenge Begins to Yield Results

   Published: 8/10/2016
8. Why a Common Diabetes Drug May Be Able to Treat a Rare Disease

   Published: 8/3/2016
9. How to Improve Patient Access to Experimental Drugs

   Published: 7/27/2016
10. Using Social Media to Find Rare Disease Patients for Clinical Trials

    Published: 7/20/2016
11. How Rare Disease Patients Weigh Risks and Benefits of a Therapy

    Published: 7/13/2016
12. Why Homology Medicines Might Be a Game Changer for Gene Therapy

    Published: 7/6/2016
13. Orchard Hopes to Bear the Fruit of Gene Therapy

    Published: 6/28/2016
14. Novel Approach to Treat Rare Disease May Lead to Drugs for Common Ones

    Published: 6/22/2016
15. Brining Whole Genome Sequencing into the Clinic

    Published: 6/15/2016
16. Bringing Patient-Centricity to Clinical Trials

    Published: 6/8/2016
17. Determining If a Child's Neurologic or Psychiatric Symptoms are Caused by an Infection

    Published: 6/1/2016
18. Making Genetic Data Accessible to Researchers

    Published: 5/25/2016
19. How New Sequencing Technology Is Changing Our Understanding of Rare Diseases

    Published: 5/18/2016
20. Marathon Readies DMD Drug for FDA

    Published: 5/11/2016