RARECast

548 Episodes

1. Expanding Access to Whole Genome Sequencing Across the Globe

   Published: 1/6/2022
2. A First-in-Class Approach to Treating a Rare and Chronic Liver Disease

   Published: 12/31/2021
3. A New Approach to Treating a Rare Endocrine Disorder

   Published: 12/24/2021
4. Detecting Genetic Disease Prior to Birth

   Published: 12/16/2021
5. Turning Words into Action: Equity, Diversity, and Inclusion in Rare Disease

   Published: 12/10/2021
6. Chasing Cures

   Published: 12/3/2021
7. A Map to Navigate A Rare Disease

   Published: 11/24/2021
8. A Popular Cancer Target Is Eyed for a Rare Immune Disorder

   Published: 11/19/2021
9. Leveraging a Gene Therapy Approach to Maximize Speed and Minimize Costs

   Published: 11/12/2021
10. Programing the Body to Make Its Own Medicine with Gene Therapy

    Published: 11/4/2021
11. Developing in Vivo Gene Editors that Target Liver Diseases

    Published: 10/28/2021
12. A Find-and-Replace Approach to Fixing the Mutation Underlying Sickle Cell Disease

    Published: 10/21/2021
13. A Bet on a Unique Set of Vectors

    Published: 10/15/2021
14. How a Rare Diagnosis Impacts a Family

    Published: 10/7/2021
15. Transforming the Rare Disease Landscape with Data

    Published: 10/1/2021
16. Creating a Playbook for Bespoke Gene Therapies

    Published: 9/24/2021
17. Finding Answers for Undiagnosed Patients with Rare Genetic Diseases

    Published: 9/16/2021
18. How a Familiar Face Can Lead to a Rare Disease Diagnosis

    Published: 9/10/2021
19. Bringing the Trial to the Patient

    Published: 9/2/2021
20. Targeting Rare and Chronic Kidney Diseases

    Published: 8/26/2021