RARECast

512 Episodes

1. Finding Answers for Undiagnosed Patients with Rare Genetic Diseases

   Published: 9/16/2021
2. How a Familiar Face Can Lead to a Rare Disease Diagnosis

   Published: 9/10/2021
3. Bringing the Trial to the Patient

   Published: 9/2/2021
4. Targeting Rare and Chronic Kidney Diseases

   Published: 8/26/2021
5. Addressing the Delivery Challenges of Genetic Medicines

   Published: 8/19/2021
6. Targeting Tissues Throughout the Body with RNA Therapies

   Published: 8/12/2021
7. Delivering Rare Disease Therapies to Patients in Need

   Published: 8/5/2021
8. An Advocate's Journey through Diagnosis, Loss, and Hope

   Published: 7/29/2021
9. Using Model Systems to Find Drugs to Repurpose for Rare Diseases

   Published: 7/22/2021
10. How a Small and Young Foundation Catalyzed Research into a Rare Disease

    Published: 7/16/2021
11. Overcoming the Limitations of Conventional Cell Engineering

    Published: 7/8/2021
12. Experimental Therapy for Rare Endocrine Disorder Offers Hope of Improved Care

    Published: 7/2/2021
13. Forging Gene Therapy Capacity and a Pipeline at the Same Time

    Published: 6/24/2021
14. Using A Natural DNA Repair Process to Improve Genetic Medicines

    Published: 6/18/2021
15. Empowering Rare Disease Patients with their Own Health Records

    Published: 6/10/2021
16. Targeting CNS Disease with Gene Therapies

    Published: 6/3/2021
17. A New Therapy Offers A Different Approach to Inhibiting the Complement System

    Published: 5/28/2021
18. Bringing Aberrant Proteins Back into the Fold

    Published: 5/20/2021
19. A Cat who Curates Rare Mice

    Published: 5/13/2021
20. Putting the Patient at the Center of Rare Disease Clinical Trials

    Published: 5/6/2021