RARECast

548 Episodes

1. Bridging the Gap Between Basic and Commercial Research for Rare Disease

   Published: 5/26/2022
2. Stoking Functional Copies of Genes to Compensate for Mutated Ones

   Published: 5/19/2022
3. Targeting ALS with Synergistic Combinations of Therapies

   Published: 5/13/2022
4. How a Polish Rare Disease Organizations Is Helping Its Ukrainian Neighbors

   Published: 5/5/2022
5. Powering a New Era of Genetic Medicine

   Published: 4/28/2022
6. Searching for a Diagnosis

   Published: 4/21/2022
7. A Novel Way to Deliver Rare Disease Therapies

   Published: 4/14/2022
8. Bringing Diversity, Equity, and Inclusion to the Books We Read

   Published: 4/7/2022
9. From Mila to Millions: Scaling N of 1 Therapies

   Published: 3/31/2022
10. Genetically Modifying Patients’ Skin Cells to Treat Rare Diseases

    Published: 3/24/2022
11. Targeting Rare, Immunologic Disorders

    Published: 3/18/2022
12. Harnessing a Natural Mechanism to Silence Disease

    Published: 3/10/2022
13. Advancing Precision Medicine with Patient Data

    Published: 3/3/2022
14. Pregnancy and Motherhood for a Woman with SMA

    Published: 2/24/2022
15. Steps to Improve Data Gathering of Rare Diseases

    Published: 2/17/2022
16. Rare Patients Learn to Make Their Voices Heard

    Published: 2/10/2022
17. Empowering Patient Organizations with Real-World Data

    Published: 2/4/2022
18. A Healthcare Communications Student Gets an Education as a Patient

    Published: 1/27/2022
19. Expanding the CRISPR Toolkit

    Published: 1/21/2022
20. Marrying Antibodies to RNA Therapies to Target Previously Inaccessible Tissues and Cells

    Published: 1/13/2022