RARECast

512 Episodes

1. Improving Narcolepsy Therapy with Drug Delivery Technology

   Published: 7/23/2020
2. Fighting the Persistent Cough in a Rare and Deadly Lung Disease

   Published: 7/15/2020
3. Targeting Huntington's Disease with Antisense

   Published: 7/8/2020
4. Assembling a Pipeline for Rare GI Disorders

   Published: 7/1/2020
5. Treating Huntington's Disease by Addressing Neuroinflammation

   Published: 6/24/2020
6. How Patient Advocate-Led Research Can Alter a Rare Disease Landscape

   Published: 6/17/2020
7. Keeping Clinical Trials Going During a Pandemic

   Published: 6/10/2020
8. Looking for Commonalities in Rare

   Published: 6/3/2020
9. Learning to Be Comfortable Being Uncomfortable

   Published: 5/27/2020
10. An Approach to De-Risk Rare Disease Drug Development

    Published: 5/20/2020
11. Targeting Epigenetics in Rare Proliferative Bone Marrow Cancers

    Published: 5/13/2020
12. Chiesi Charges Ahead in Rare Disease

    Published: 5/6/2020
13. Targeting the Metabolism of Rare Cancers

    Published: 4/29/2020
14. Unlocking Bryson's Brain

    Published: 4/22/2020
15. Living Therapies for Chronic Conditions

    Published: 4/15/2020
16. A One-to-Many Approach to Gene Therapy for Retinal Disease

    Published: 4/8/2020
17. Targeting an Immune Switch in Rare Diseases

    Published: 4/1/2020
18. Targeting the Regulatory Genome to Treat Rare Blood Diseases

    Published: 3/25/2020
19. A Reborn Forma Therapeutics Focuses on Rare Blood Diseases and Cancer

    Published: 3/18/2020
20. Targeting Genetic Diseases at Their Root Cause

    Published: 3/11/2020