RARECast

516 Episodes

1. Delivering Injectable Drugs Orally

   Published: 8/20/2020
2. What Young Adults with Rare Conditions Need to Know About Health Insurance

   Published: 8/14/2020
3. Mirum Prepares to Seek Approval for Rare Liver Disease Therapy

   Published: 8/7/2020
4. Payer Perceptions of Fairness in Pricing Rare Disease Therapies

   Published: 8/4/2020
5. Improving Narcolepsy Therapy with Drug Delivery Technology

   Published: 7/23/2020
6. Fighting the Persistent Cough in a Rare and Deadly Lung Disease

   Published: 7/15/2020
7. Targeting Huntington's Disease with Antisense

   Published: 7/8/2020
8. Assembling a Pipeline for Rare GI Disorders

   Published: 7/1/2020
9. Treating Huntington's Disease by Addressing Neuroinflammation

   Published: 6/24/2020
10. How Patient Advocate-Led Research Can Alter a Rare Disease Landscape

    Published: 6/17/2020
11. Keeping Clinical Trials Going During a Pandemic

    Published: 6/10/2020
12. Looking for Commonalities in Rare

    Published: 6/3/2020
13. Learning to Be Comfortable Being Uncomfortable

    Published: 5/27/2020
14. An Approach to De-Risk Rare Disease Drug Development

    Published: 5/20/2020
15. Targeting Epigenetics in Rare Proliferative Bone Marrow Cancers

    Published: 5/13/2020
16. Chiesi Charges Ahead in Rare Disease

    Published: 5/6/2020
17. Targeting the Metabolism of Rare Cancers

    Published: 4/29/2020
18. Unlocking Bryson's Brain

    Published: 4/22/2020
19. Living Therapies for Chronic Conditions

    Published: 4/15/2020
20. A One-to-Many Approach to Gene Therapy for Retinal Disease

    Published: 4/8/2020