RARECast

512 Episodes

1. Targeting Hormone Dysregulation in Prader-Willi Syndrome

   Published: 3/4/2020
2. Rare Disease Advocates Take to the Hill

   Published: 2/25/2020
3. Targeting a Common Link in Otherwise Different Rare Diseases

   Published: 2/19/2020
4. Bringing Clinical Trials to Patients

   Published: 2/12/2020
5. Crowdsourcing Therapeutic Approaches for an Ultra-Rare Disease

   Published: 2/5/2020
6. Delivering Oligonucleotide Therapies to Any Cell Type

   Published: 1/29/2020
7. Protalix Looks Beyond Biobetters

   Published: 1/22/2020
8. Driving N-of-1 Therapies for Ultra-Rare Disease Patients

   Published: 1/15/2020
9. Cutting the Time and Cost of Drug Discovery with MicroOrgans

   Published: 1/8/2020
10. Acquisition Combines Two Pipelines for Rare Skin Diseases

    Published: 1/2/2020
11. Programming Cells to Produce Neuroprotective Factors to Treat ALS

    Published: 12/26/2019
12. Origin's Rapid Path to Seek Approval for Treatment of Ultra-Rare Metabolic Condition

    Published: 12/18/2019
13. Developing a Common Language for Rare Diseases

    Published: 12/11/2019
14. Why Payers Lag Drug Developers and Regulators in Embracing Real-World Evidence

    Published: 12/4/2019
15. How a Brother's Love Is Forging a Path for Customized Therapies for Rare Disease Patients

    Published: 11/27/2019
16. Addressing the Barriers to Accessing Experimental Therapies

    Published: 11/20/2019
17. A Journey to Advocacy

    Published: 11/13/2019
18. Turning Chronic Illness into a Fashion Statement

    Published: 11/6/2019
19. Connecting Young Adults with Rare and Chronic Conditions

    Published: 10/30/2019
20. Helping Caregivers Care for Themselves

    Published: 10/23/2019