RARECast

548 Episodes

1. Crowdsourcing Therapeutic Approaches for an Ultra-Rare Disease

   Published: 2/5/2020
2. Delivering Oligonucleotide Therapies to Any Cell Type

   Published: 1/29/2020
3. Protalix Looks Beyond Biobetters

   Published: 1/22/2020
4. Driving N-of-1 Therapies for Ultra-Rare Disease Patients

   Published: 1/15/2020
5. Cutting the Time and Cost of Drug Discovery with MicroOrgans

   Published: 1/8/2020
6. Acquisition Combines Two Pipelines for Rare Skin Diseases

   Published: 1/2/2020
7. Programming Cells to Produce Neuroprotective Factors to Treat ALS

   Published: 12/26/2019
8. Origin's Rapid Path to Seek Approval for Treatment of Ultra-Rare Metabolic Condition

   Published: 12/18/2019
9. Developing a Common Language for Rare Diseases

   Published: 12/11/2019
10. Why Payers Lag Drug Developers and Regulators in Embracing Real-World Evidence

    Published: 12/4/2019
11. How a Brother's Love Is Forging a Path for Customized Therapies for Rare Disease Patients

    Published: 11/27/2019
12. Addressing the Barriers to Accessing Experimental Therapies

    Published: 11/20/2019
13. A Journey to Advocacy

    Published: 11/13/2019
14. Turning Chronic Illness into a Fashion Statement

    Published: 11/6/2019
15. Connecting Young Adults with Rare and Chronic Conditions

    Published: 10/30/2019
16. Helping Caregivers Care for Themselves

    Published: 10/23/2019
17. A Festival of Moving Pictures

    Published: 10/16/2019
18. Deep Genomics Boasts an AI First in Drug Discovery

    Published: 10/9/2019
19. How to Live with a Disability with Your Mojo Intact

    Published: 10/3/2019
20. Why a Big Pharma Exec Embraced Rare Neurological Diseases

    Published: 9/25/2019