RARECast

548 Episodes

1. Fighting for Other People's Children

   Published: 9/18/2019
2. A Doctor's Quest to Cure His Own Rare Disease

   Published: 9/11/2019
3. Susannah Cahalan and her Month of Madness

   Published: 9/4/2019
4. The Benefits Support Groups Offer Rare Disease Patients

   Published: 8/29/2019
5. Targeting the Epigenetic Drivers of Cancer

   Published: 8/21/2019
6. Tackling Kidney Diseases with Orally-Delivered Enzymes

   Published: 8/14/2019
7. Giving Voice to Patients through Data

   Published: 8/8/2019
8. Seeking to Halt and Reverse Fibrotic Diseases

   Published: 7/31/2019
9. Addressing the Complexities of Rare Disease with Centers of Excellence

   Published: 7/24/2019
10. Using Cell Therapies to Restore Power in Mitochondrial Diseases

    Published: 7/17/2019
11. Passage Bio Betting on Penn Connection to Give It an Edge in Developing Gene Therapies

    Published: 7/10/2019
12. Finding Appropriate Endpoints and Measures for Rare Eye Diseases

    Published: 7/3/2019
13. Marrying Antibodies and Oligonucleotides to Target Genetic Medicine

    Published: 6/26/2019
14. What Rare Disease Patients Should Understand about Genetics

    Published: 6/19/2019
15. Program Seeks to Drive Collaborative Research Model Among Rare Disease Groups

    Published: 6/12/2019
16. A Gene Hunter Becomes a Drug Hunter Too

    Published: 6/5/2019
17. The Psychological Toll Rare Diseases Can Have on Healthy Siblings

    Published: 5/29/2019
18. Blood Test Can Provide Earlier Diagnosis of Autism Spectrum Disorder

    Published: 5/22/2019
19. Understanding the Role of Natural History Studies in Clinical Trials

    Published: 5/15/2019
20. How Two Mothers Discovered That a Drug for One Rare Disorder Might Benefit Another

    Published: 5/8/2019