RARECast

516 Episodes

1. Establishing Clinical Standards for a Rare Disease

   Published: 9/19/2018
2. Teen Rare Disease Advocate Fights the Condition That Took His Brother's Life

   Published: 9/12/2018
3. Addressing the Emotional Toll of Rare Diseases

   Published: 9/5/2018
4. Forging a Research Agenda for a Rare Disease

   Published: 8/29/2018
5. Living with an Uncertain Rare Diagnosis

   Published: 8/22/2018
6. A Rare Disease Advocate Teaches Doctors to See and Speak Differently

   Published: 8/17/2018
7. The Caregiver Who Cried in the Shower

   Published: 8/8/2018
8. Curating Patient Data to Accelerate Rare Disease Drug Development

   Published: 8/1/2018
9. Forging a Research Agenda for a Rare Disease

   Published: 7/25/2018
10. Making the Journey from All-American Athlete to Rare Disease Advocate

    Published: 7/18/2018
11. How Destiny Lamonte Learned to Advocate for Herself and Others

    Published: 7/11/2018
12. Where the NIH Does Its Banking

    Published: 7/5/2018
13. Making Sense of Nonsense Mutations

    Published: 6/27/2018
14. Rewriting Faulty RNA

    Published: 6/20/2018
15. Experimental Drug for "Elephant Man" Disease May Benefit Certain Cancers Too

    Published: 6/13/2018
16. Programming Stem Cells to Protect Neurons in ALS and other Neurodegenerative Conditions

    Published: 6/6/2018
17. Why a Topical, Off-the-Shelf, Gene Therapy May Hold Promise for a Rare Skin Condition

    Published: 5/30/2018
18. An Ironman Champion with Cystic Fibrosis Discusses her Changing Relationship with Her Disease

    Published: 5/23/2018
19. Why an Experimental Fragile X Drug May Treat a Range of Neurodegenerative Diseases

    Published: 5/16/2018
20. The Case for a Daily Self-Injection to Treat Hemophilia

    Published: 5/9/2018