RARECast

512 Episodes

1. Targeting Neuroinflammation to Treat ALS

   Published: 8/17/2023
2. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

   Published: 8/10/2023
3. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

   Published: 8/3/2023
4. Inhibiting Electrical Activity in Rare, Seizure Disorders

   Published: 7/27/2023
5. Improving the Function and Usability of Clothing for People with Disabilities

   Published: 7/20/2023
6. Treating Cardiopulmonary Disease with Inhaled Targeted Therapies

   Published: 7/13/2023
7. An Ally for the Undiagnosed Emerges

   Published: 6/29/2023
8. A Patient-Driven Registry Focused on Health-Related Quality of Life Data

   Published: 6/29/2023
9. Help for Rare Disease Patients That’s Just a Click Away

   Published: 6/22/2023
10. Diagnosing Autism with a Single Strand of Hair

    Published: 6/15/2023
11. Bringing Regenerative Medicine to a Rare Bone Condition in Children

    Published: 6/8/2023
12. Bringing Precision to CRISPR-Based Genome Editing

    Published: 6/1/2023
13. Capturing Patients’ Experience in Their Daily Lives

    Published: 5/25/2023
14. From One to Many

    Published: 5/18/2023
15. A Nasal Spray to Curb Excessive Eating in Prader-Willi

    Published: 5/11/2023
16. How One Foundation Is Laying the Groundwork to Advance Treatments for an Ultra-Rare Disease

    Published: 5/4/2023
17. Forging a New Path for Medicine

    Published: 4/27/2023
18. Restoring Hearing through Gene Therapies

    Published: 4/20/2023
19. Creating a Sustainable Reimbursement Model for Ultra-Rare Therapies

    Published: 4/13/2023
20. Lumos Hopes Its Oral Alternative to HGH Will Fuel Its Growth

    Published: 4/5/2023