RARECast

548 Episodes

1. Accelerating the Development of Genetic Medicines with AI

   Published: 12/7/2023
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Published: 11/30/2023
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Published: 11/22/2023
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Published: 11/16/2023
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Published: 11/9/2023
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Published: 11/2/2023
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Published: 10/26/2023
8. Turning Grief into Action

   Published: 10/19/2023
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Published: 10/12/2023
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Published: 10/5/2023
11. A Genetic Counselor’s Journey into Patient Advocacy

    Published: 9/28/2023
12. A Company in the Fold of Rare Disease

    Published: 9/21/2023
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Published: 9/14/2023
14. Keeping the Sentinels of the Brain Vigilant

    Published: 9/7/2023
15. Considering the Unfinished Work in Cystic Fibrosis

    Published: 8/31/2023
16. How to Advocate for Yourself as You Battle Cancer

    Published: 8/24/2023
17. Targeting Neuroinflammation to Treat ALS

    Published: 8/17/2023
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Published: 8/10/2023
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Published: 8/3/2023
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Published: 7/27/2023