RARECast

548 Episodes

1. Improving the Function and Usability of Clothing for People with Disabilities

   Published: 7/20/2023
2. Treating Cardiopulmonary Disease with Inhaled Targeted Therapies

   Published: 7/13/2023
3. An Ally for the Undiagnosed Emerges

   Published: 6/29/2023
4. A Patient-Driven Registry Focused on Health-Related Quality of Life Data

   Published: 6/29/2023
5. Help for Rare Disease Patients That’s Just a Click Away

   Published: 6/22/2023
6. Diagnosing Autism with a Single Strand of Hair

   Published: 6/15/2023
7. Bringing Regenerative Medicine to a Rare Bone Condition in Children

   Published: 6/8/2023
8. Bringing Precision to CRISPR-Based Genome Editing

   Published: 6/1/2023
9. Capturing Patients’ Experience in Their Daily Lives

   Published: 5/25/2023
10. From One to Many

    Published: 5/18/2023
11. A Nasal Spray to Curb Excessive Eating in Prader-Willi

    Published: 5/11/2023
12. How One Foundation Is Laying the Groundwork to Advance Treatments for an Ultra-Rare Disease

    Published: 5/4/2023
13. Forging a New Path for Medicine

    Published: 4/27/2023
14. Restoring Hearing through Gene Therapies

    Published: 4/20/2023
15. Creating a Sustainable Reimbursement Model for Ultra-Rare Therapies

    Published: 4/13/2023
16. Lumos Hopes Its Oral Alternative to HGH Will Fuel Its Growth

    Published: 4/5/2023
17. Advancing a Gene Therapy for a Rare and Fatal CNS Disorder

    Published: 3/30/2023
18. Addressing the Barriers to Patient Participation in Clinical Trials

    Published: 3/23/2023
19. A Venture Philanthropist Makes the Case for Advocates Taking Equity

    Published: 3/16/2023
20. Seeking a Sustainable Business Developing on N-of-1 Therapies

    Published: 3/9/2023