RARECast

512 Episodes

1. Empowering Patient Organizations with Real-World Data

   Published: 2/4/2022
2. A Healthcare Communications Student Gets an Education as a Patient

   Published: 1/27/2022
3. Expanding the CRISPR Toolkit

   Published: 1/21/2022
4. Marrying Antibodies to RNA Therapies to Target Previously Inaccessible Tissues and Cells

   Published: 1/13/2022
5. Expanding Access to Whole Genome Sequencing Across the Globe

   Published: 1/6/2022
6. A First-in-Class Approach to Treating a Rare and Chronic Liver Disease

   Published: 12/31/2021
7. A New Approach to Treating a Rare Endocrine Disorder

   Published: 12/24/2021
8. Detecting Genetic Disease Prior to Birth

   Published: 12/16/2021
9. Turning Words into Action: Equity, Diversity, and Inclusion in Rare Disease

   Published: 12/10/2021
10. Chasing Cures

    Published: 12/3/2021
11. A Map to Navigate A Rare Disease

    Published: 11/24/2021
12. A Popular Cancer Target Is Eyed for a Rare Immune Disorder

    Published: 11/19/2021
13. Leveraging a Gene Therapy Approach to Maximize Speed and Minimize Costs

    Published: 11/12/2021
14. Programing the Body to Make Its Own Medicine with Gene Therapy

    Published: 11/4/2021
15. Developing in Vivo Gene Editors that Target Liver Diseases

    Published: 10/28/2021
16. A Find-and-Replace Approach to Fixing the Mutation Underlying Sickle Cell Disease

    Published: 10/21/2021
17. A Bet on a Unique Set of Vectors

    Published: 10/15/2021
18. How a Rare Diagnosis Impacts a Family

    Published: 10/7/2021
19. Transforming the Rare Disease Landscape with Data

    Published: 10/1/2021
20. Creating a Playbook for Bespoke Gene Therapies

    Published: 9/24/2021