RARECast

516 Episodes

1. Advancing Precision Medicine with Patient Data

   Published: 3/3/2022
2. Pregnancy and Motherhood for a Woman with SMA

   Published: 2/24/2022
3. Steps to Improve Data Gathering of Rare Diseases

   Published: 2/17/2022
4. Rare Patients Learn to Make Their Voices Heard

   Published: 2/10/2022
5. Empowering Patient Organizations with Real-World Data

   Published: 2/4/2022
6. A Healthcare Communications Student Gets an Education as a Patient

   Published: 1/27/2022
7. Expanding the CRISPR Toolkit

   Published: 1/21/2022
8. Marrying Antibodies to RNA Therapies to Target Previously Inaccessible Tissues and Cells

   Published: 1/13/2022
9. Expanding Access to Whole Genome Sequencing Across the Globe

   Published: 1/6/2022
10. A First-in-Class Approach to Treating a Rare and Chronic Liver Disease

    Published: 12/31/2021
11. A New Approach to Treating a Rare Endocrine Disorder

    Published: 12/24/2021
12. Detecting Genetic Disease Prior to Birth

    Published: 12/16/2021
13. Turning Words into Action: Equity, Diversity, and Inclusion in Rare Disease

    Published: 12/10/2021
14. Chasing Cures

    Published: 12/3/2021
15. A Map to Navigate A Rare Disease

    Published: 11/24/2021
16. A Popular Cancer Target Is Eyed for a Rare Immune Disorder

    Published: 11/19/2021
17. Leveraging a Gene Therapy Approach to Maximize Speed and Minimize Costs

    Published: 11/12/2021
18. Programing the Body to Make Its Own Medicine with Gene Therapy

    Published: 11/4/2021
19. Developing in Vivo Gene Editors that Target Liver Diseases

    Published: 10/28/2021
20. A Find-and-Replace Approach to Fixing the Mutation Underlying Sickle Cell Disease

    Published: 10/21/2021